Generic selectors
Exact matches only
Search in title
Search in content
Post Type Selectors

FDA Approves First Gene Therapy for Non-Muscle-Invasive Bladder Cancer

The FDA has approved nadofaragene firadenovec (Adstiladrin) as the first gene therapy for the treatment of high-risk bacillus Calmette-Guérin (BCG)-unresponsive non-muscle-invasive bladder cancer (NMIBC), the agency announced on Friday. An adenoviral vector-based product, nadofaragene firadenovec, is specifically indicated for adult patients with carcinoma in situ (CIS) with or without papillary tumors. Approval was based on […]

Opinion | I’m a Doctor and I’ve Been Sober for a Year

My first COVID vacation last year was spectacular, except that I barely remember 3 days of it because I was drinking to the point of amnesia. I am a physician from a multigenerational family of alcoholics, and I never wanted to struggle with alcohol use disorder (AUD). Instead, I discovered that I could avoid feelings […]

FDA OKs First Gene Therapy for Hemophilia B

The FDA on Tuesday approved the first gene therapy for treating hemophilia B, a genetic bleeding disorder resulting from missing or insufficient levels of factor IX. Etranacogene dezaparvovec (Hemgenix) is indicated for adults with the condition who currently use factor IX prophylaxis therapy for blood clotting, those who have or have had life-threatening hemorrhage, or […]

A better model for type 2 diabetes: The Nile rat

Researchers have assembled the first reference genome for the Nile rat — a kind of genetic template of this species that may be used for laboratory and clinical studies. The hope, according to UC Santa Barbara researcher Huishi Toh, is that it will be useful for those who investigate Type 2 diabetes and neurological disorders […]

Promising Results in First Test of In Utero Enzyme-Replacement Therapy

The first test of in utero enzyme replacement therapy (ERT) proved safe and effective for a baby with infantile-onset Pompe disease, according to a case report. An infant with cross-reactive immunologic material (CRIM)-negative infantile-onset Pompe disease — the most severe end of the disease spectrum — had no cardiac manifestations following treatment, compared to her […]

Diet high in saturated fat can reprogram immune cells in mice

A new study by Portland State University researchers is the first to show that eating a diet exclusively high in saturated fats can reprogram the mouse immune system, making it better able to fight off infection but more susceptible to systemic inflammatory conditions, including sepsis. Brooke Napier, assistant professor of biology at PSU, led the […]

DBN Health News